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Community register of orphan medicinal products


Product information

Exon 53 specific phosphorothioate oligonucleotide

EU orphan designation number: EU/3/12/992   
Active ingredient: Exon 53 specific phosphorothioate oligonucleotide
Indication: Treatment of Duchenne muscular dystrophy
Sponsor: BioMarin International Limited
6th Floor, 2 Grand Canal Square, Dublin 2, Ireland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
01/05/2012 Orphan designation EMA/OD/143/11 (2012)2988 of 26/04/2012
09/06/2015 Transfer of orphan designation EMA/OD/143/11/T/01 (2015)3929 of 05/06/2015
01/12/2016 Change of name and/or address of sponsor