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Pharmaceuticals - Union Register


Register of orphan medicinal products


Product information

Exon 45 specific phosphorothioate oligonucleotide

EU orphan designation number: EU/3/12/991   
Active ingredient: Exon 45 specific phosphorothioate oligonucleotide
Indication: Treatment of Duchenne muscular dystrophy
Sponsor: BioMarin International Limited
6th Floor, 2 Grand Canal Square, Dublin 2, Ireland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
1/05/2012 Orphan designation EMA/OD/142/11 (2012)2987 of 26/04/2012
9/06/2015 Transfer of orphan designation EMA/OD/142/11/T/01 (2015)3928 of 5/06/2015
1/12/2016 Change of name and/or address of sponsor