- General information enquiries
- Call 00 800 6 7 8 9 10 11
- E-mail your questions

European Commission
Public Health
Accessibility tools
Service tools
Language selector
- Current languageen
Navigation path
- European Commission
- Public health
- Register
- Orphan products
- Adeno-associated viral vector containing the human alpha-N-a
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Adeno-associated viral vector containing the human alpha-N-acetylglucosaminidase gene
Public summary of scientific opinion
European Commission procedures |
Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
02/11/2011 | Orphan designation | EMA/OD/065/11 | (2011)7895 of 27/10/2011 |