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- Adeno-associated viral vector containing the human alpha-N-a
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Adeno-associated viral vector containing the human alpha-N-acetylglucosaminidase gene
| EU orphan designation number: | EU/3/11/917
|
| Active ingredient: | Adeno-associated viral vector containing the human alpha-N-acetylglucosaminidase gene |
| Indication: | Treatment of mucopolysaccharidosis type IIIB (Sanfilippo B syndrome) |
| Sponsor: | Institut Pasteur
25-28 rue du Docteur Roux, 75724 Paris CEDEX 15, France |
Public summary of scientific opinion
European Commission procedures |
| Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
| 02/11/2011 | Orphan designation | EMA/OD/065/11 | (2011)7895 of 27/10/2011 |
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