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Community register of orphan medicinal products


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Product information

Adeno-associated viral vector serotype 9 containing the human sulfamidase gene

EU orphan designation number: EU/3/11/877   
Active ingredient: Adeno-associated viral vector serotype 9 containing the human sulfamidase gene
Indication: Treatment of mucopolysaccharidosis type IIIA (Sanfilippo A syndrome)
Sponsor: Laboratorios del Dr Esteve, S.A.
Av. Mare de Déu de Montserrat 221, 08041 Barcelona, España

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
27/06/2011 Orphan designation EMA/OD/171/10 (2011)4551 of 21/06/2011