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Pharmaceuticals - Community Register

  

Community register of orphan medicinal products


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Product information

Adeno-associated viral vector containing the human ARSB gene

EU orphan designation number: EU/3/11/864   
Active ingredient: Adeno-associated viral vector containing the human ARSB gene
Indication: Treatment of mucopolysaccharidosis type VI (Maroteaux-Lamy syndrome)
Sponsor: Fondazione Telethon
Via Varese 16, 00185 Roma, Italia

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
17/05/2011 Orphan Designation EMA/OD/147/10 (2011)3490 of 13/05/2011
11/10/2013 Change of address of sponsor
17/12/2014 Change of address of sponsor