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Community register of orphan medicinal products


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Adenovirus-associated viral vector serotype 10 carrying the human N-sulfoglucosamine sulfohydrolase and sulfatase modifying factor 1 cDNAs

EU orphan designation number: EU/3/10/772   
Active ingredient: Adenovirus-associated viral vector serotype 10 carrying the human N-sulfoglucosamine sulfohydrolase and sulfatase modifying factor 1 cDNAs
Indication: Treatment of mucopolysaccharidosis, type IIIA (Sanfilippo A syndrome)
Sponsor: LYSOGENE
52 rue La Boetie, 75008 Paris, France

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
22/09/2010 Orphan designation EMA/OD/042/10 (2010)6639 of 20/09/2010
24/05/2012 Change of name and/or address of sponsor EMA/OD/042/10
10/02/2015 Change of name and/or address of sponsor