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Community register of orphan medicinal products


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Adenovirus-associated viral vector serotype 10 carrying the human N-sulfoglucosamine sulfohydrolase and sulfatase modifying factor 1 cDNAs

EU orphan designation number: EU/3/10/772   
Active ingredient: Adenovirus-associated viral vector serotype 10 carrying the human N-sulfoglucosamine sulfohydrolase and sulfatase modifying factor 1 cDNAs
Indication: Treatment of mucopolysaccharidosis, type IIIA (Sanfilippo A syndrome)
Sponsor: LYSOGENE
52 rue La Boetie, F-75008 Paris, France

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
22/09/2010 Orphan Designation EMA/OD/042/10 (2010)6639 of 20/09/2010
24/05/2012 Change name of sponsor EMA/OD/042/10
10/02/2015 Change of address of sponsor