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Pharmaceuticals - Community Register

  

Community register of orphan medicinal products


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Product information

Adeno-associated viral vector containing porphobilinogen deaminase gene

EU orphan designation number: EU/3/09/632   
Active ingredient: Adeno-associated viral vector containing porphobilinogen deaminase gene
Indication: Treatment of acute intermittent porphyria
Sponsor: uniQure Biopharma B.V.
Paasheuvelweg 25, 1105 BP, Amsterdam, Nederland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
05/05/2009 Orphan designation EMEA/OD/102/08 (2009)3458 of 29/04/2009
17/07/2012 Change of name and/or address of sponsor EMEA/OD/102/08
22/05/2017 Change of name and/or address of sponsor