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Community register of orphan medicinal products


Product information

Exon 44 specific phosphorothioate oligonucleotide

EU orphan designation number: EU/3/08/598   
Active ingredient: Exon 44 specific phosphorothioate oligonucleotide
Indication: Treatment of Duchenne muscular dystrophy
Sponsor: BioMarin International Limited
6th Floor, 2 Grand Canal Square, Dublin 2, Ireland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
03/03/2009 Orphan designation EMEA/OD/081/08 (2009)1519 of 27/02/2009
09/01/2012 Change of name and/or address of sponsor EMEA/OD/081/08
09/06/2015 Transfer of orphan designation EMA/OD/081/08/T/01 (2015)3925 of 05/06/2015