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Register of orphan medicinal products


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Autologous CD34+ cells transfected with lentiviral vector containing the human arylsulfatase A cDNA

EU orphan designation number: EU/3/07/446   
Active ingredient: Autologous CD34+ cells transfected with lentiviral vector containing the human arylsulfatase A cDNA
Indication: Treatment of metachromatic leukodystrophy
Sponsor: Orchard Therapeutics (Netherlands) B.V.
Prins Bernhardplein 200, 1097 JB, Noord-Holland, Amsterdam, Nederland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
17/04/2007 Orphan designation EMEA/OD/102/06 (2007)1769 of 13/04/2007
2/12/2009 Change of name and/or address of sponsor
11/10/2013 Change of name and/or address of sponsor
1/08/2014 Transfer of orphan designation EMA/OD/102/06/T/01 (2014)5574 of 30/07/2014
2/08/2018 Transfer of orphan designation EMA/OD/102/06/T/02 (2018)5287 of 31/07/2018
11/03/2019 Change of name and/or address of sponsor
29/03/2019 Transfer of orphan designation EMA/OD/0000003632 (2019)2430 of 25/03/2019