Pharmaceuticals - Union Register

  

Register of orphan medicinal products


GRANTED  

Product information

Miglustat

EU orphan designation number: EU/3/18/2129   
Active ingredient: Miglustat
Indication: Treatment of glycogen storage disease type II (Pompe's disease)
Sponsor: Amicus Therapeutics UK Ltd
Phoenix House, Oxford Road, Tatling End, Gerrards Cross, Buckinghamshire SL9 7AP, United Kingdom

  

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
17/01/2019 Orphan designation EMA/OD/0000002050 (2019)225 of 11/01/2019