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Register of orphan medicinal products


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Adeno-associated viral vector serotype hu68 containing the human SMN1 gene

EU orphan designation number: EU/3/18/2060   
Active ingredient: Adeno-associated viral vector serotype hu68 containing the human SMN1 gene
Indication: Treatment of spinal muscular atrophy
Sponsor: Biogen Idec Limited
Innovation House, 70 Norden Road, Maidenhead, Berkshire SL6 4AY, United Kingdom

  

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
28/08/2018 Orphan designation EMA/OD/065/18 (2018)5732 of 24/08/2018