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Pharmaceuticals - Union Register

  

Register of orphan medicinal products


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Product information

N-acetylgalactosamine-conjugated synthetic double-stranded oligomer specific to serpin family A member 1 gene

EU orphan designation number: EU/3/18/2048   
Active ingredient: N-acetylgalactosamine-conjugated synthetic double-stranded oligomer specific to serpin family A member 1 gene
Indication: Treatment of congenital alpha-1 antitrypsin deficiency
Sponsor: Pharma Gateway AB
Johanneslundsvägen 2, Hammarby, 194 61 Upplands Väsby, Stockholms Lan, Sverige

  

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
2/08/2018 Orphan designation EMA/OD/061/18 (2018)5280 of 31/07/2018