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Pharmaceuticals - Union Register

  

Register of orphan medicinal products


GRANTED  

Product information

Recombinant adeno-associated viral vector serotype 9 containing human iduronidase gene

EU orphan designation number: EU/3/18/2039   
Active ingredient: Recombinant adeno-associated viral vector serotype 9 containing human iduronidase gene
Indication: Treatment of mucopolysaccharidosis type I
Sponsor: REGENXBIO EU Limited
25-28 North Wall Quay, Dublin 1 D01H104, Ireland

  

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
29/06/2018 Orphan designation EMA/OD/027/18 (2018)4184 of 27/06/2018