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Pharmaceuticals - Union Register

  

Register of orphan medicinal products


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Codon-optimised human ornithine transcarbamylase mRNA complexed with lipid-based nanoparticles

EU orphan designation number: EU/3/18/2033   
Active ingredient: Codon-optimised human ornithine transcarbamylase mRNA complexed with lipid-based nanoparticles
Indication: Treatment of ornithine transcarbamylase deficiency
Sponsor: Real Regulatory Limited
Unit 9A, Plato Business Park, Damastown, Dublin 15, D15 PA4C, Ireland

  

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
29/06/2018 Orphan designation EMA/OD/022/18 (2018)4178 of 27/06/2018