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Modified messenger ribonucleic acid encoding human ornithine transcarbamylase enzyme encapsulated into lipid nanoparticles

EU orphan designation number: EU/3/17/1867   
Active ingredient: Modified messenger ribonucleic acid encoding human ornithine transcarbamylase enzyme encapsulated into lipid nanoparticles
Indication: Treatment of ornithine transcarbamylase deficiency
Sponsor: PhaseRx Ireland, Ltd
20 Harcourt Street, Dublin 2, D02 H364, Ireland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
24/04/2017 Orphan designation EMA/OD/326/16 (2017)2786 of 20/04/2017