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Adeno-associated viral vector serotype rh.10 expressing beta-galactosidase

EU orphan designation number: EU/3/17/1851   
Active ingredient: Adeno-associated viral vector serotype rh.10 expressing beta-galactosidase
Indication: Treatment of GM1 gangliosidosis
Sponsor: LYSOGENE
18-20 rue Jacques Dulud, 92200 Neuilly-sur-Seine, France

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
22/03/2017 Orphan designation EMA/OD/265/16 (2017)1978 of 20/03/2017