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- Recombinant adeno-associated viral vector serotype 9 contain
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Recombinant adeno-associated viral vector serotype 9 containing the human N-alpha-acetylglucosaminidase gene
| EU orphan designation number: | EU/3/16/1825
|
| Active ingredient: | Recombinant adeno-associated viral vector serotype 9 containing the human N-alpha-acetylglucosaminidase gene |
| Indication: | Treatment of mucopolysaccharidosis type IIIB (Sanfilippo B syndrome) |
| Sponsor: | Ser-mes Planificación SL
Rufino González 14, Esc.1ª-2ºD, 28037 Madrid, España |
European Commission procedures |
| Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
| 16/01/2017 | Orphan designation | EMA/OD/226/16 | (2017)230 of 12/01/2017 |
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