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- Recombinant self-complementary adeno-associated viral vector
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Recombinant self-complementary adeno-associated viral vector serotype 9 containing the human CLN3 gene
| EU orphan designation number: | EU/3/16/1806
|
| Active ingredient: | Recombinant self-complementary adeno-associated viral vector serotype 9 containing the human CLN3 gene |
| Indication: | Treatment of neuronal ceroid lipofuscinosis |
| Sponsor: | Ser-mes Planificación SL
Rufino González 14, Esc.1ª-2ºD, 28037 Madrid, España |
Public summary of scientific opinion
European Commission procedures |
| Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
| 14/12/2016 | Orphan designation | EMA/OD/195/16 | (2016)8706 of 12/12/2016 |
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