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- Modified mRNA encoding the UGT1A1 protein
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Modified mRNA encoding the UGT1A1 protein
| EU orphan designation number: | EU/3/16/1684
|
| Active ingredient: | Modified mRNA encoding the UGT1A1 protein |
| Indication: | Treatment of Crigler-Najjar syndrome |
| Sponsor: | Alexion Europe SAS
1-15 avenue Edouard Belin, 92500 Rueil-Malmaison, France |
Public summary of scientific opinion
European Commission procedures |
| Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
| 29/06/2016 | Orphan designation | EMA/OD/047/16 | (2016)4125 of 27/06/2016 |
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