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- Recombinant adeno-associated viral vector containing the hum
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Recombinant adeno-associated viral vector containing the human RPGR gene
| EU orphan designation number: | EU/3/16/1665
|
| Active ingredient: | Recombinant adeno-associated viral vector containing the human RPGR gene |
| Indication: | Treatment of retinitis pigmentosa caused by mutations in the RPGR gene |
| Sponsor: | TMC Pharma Services Ltd
Lodge Farm Barn, Elvetham Park Estate, Fleet Road, Hartley Wintney, Hampshire RG27 8AS, United Kingdom |
Public summary of scientific opinion
European Commission procedures |
| Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
| 01/06/2016 | Orphan designation | EMA/OD/002/16 | (2016)3421 of 30/05/2016 |
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