Pharmaceuticals - Union Register


Register of orphan medicinal products


Product information


EU orphan designation number: EU/3/15/1525   
Active ingredient: Triheptanoin
Indication: Treatment of mitochondrial trifunctional protein deficiency
Sponsor: Ultragenyx Netherlands B.V.
Evert van de Beekstraat 104, Schiphol Airport - The Base B, 1118CN Schiphol, Nederland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
30/07/2015 Orphan designation EMA/OD/047/15 (2015)5432 of 28/07/2015
14/02/2019 Transfer of orphan designation EMA/OD/0000003845 (2019)1368 of 12/02/2019