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Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA

EU orphan designation number: EU/3/14/1389   
Active ingredient: Adeno-associated viral vector serotype rh.10 carrying the human N-sulfoglucosamine sulfohydrolase cDNA
Indication: Treatment of mucopolysaccharidosis type IIIA (Sanfilippo A syndrome)
Sponsor: LYSOGENE
18-20 rue Jacques Dulud, 92200 Neuilly-sur-Seine, France

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
18/12/2014 Orphan designation EMA/OD/164/14 (2014)10037 of 16/12/2014
8/04/2015 Corrigendum (2015)2368 of 1/04/2015