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- Lentiviral vector containing the human liver and erythroid p
Pharmaceuticals - Community Register
Community register of orphan medicinal products | GRANTED |
Product information |
Lentiviral vector containing the human liver and erythroid pyruvate kinase (PKLR) gene
| EU orphan designation number: | EU/3/14/1330
|
| Active ingredient: | Lentiviral vector containing the human liver and erythroid pyruvate kinase (PKLR) gene |
| Indication: | Treatment of pyruvate kinase deficiency |
| Sponsor: | Centro de Investigación Biomédica en Red (CIBER)
Instituto de Salud Carlos III, Pabellón 11, Planta 0, C/ Monforte de Lemos 3-5, 28029 Madrid, España |
Public summary of scientific opinion
European Commission procedures |
| Close date procedure | Procedure type | EMEA number | Decision | summary publ | decision docs | annex |
| 26/08/2014 | Orphan designation | EMA/OD/102/14 | (2014)6135 of 22/08/2014 |
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