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Community register of orphan medicinal products


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Product information

Mixture of two adeno-associated viral vectors of serotype 8 containing the 5'-half sequence of human MYO7A gene and the 3'-half sequence of human MYO7A gene

EU orphan designation number: EU/3/14/1282   
Active ingredient: Mixture of two adeno-associated viral vectors of serotype 8 containing the 5'-half sequence of human MYO7A gene and the 3'-half sequence of human MYO7A gene
Indication: Treatment of Usher syndrome
Sponsor: Fondazione Telethon
Via Varese 16, 00185 Roma, Italia

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page
Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
08/07/2014 Orphan designation EMA/OD/004/14 (2014)4834 of 04/07/2014
17/12/2014 Change of name and/or address of sponsor