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Autologous CD34+ haematopoietic stem cells transduced with lentiviral vector encoding the human beta A-T87Q-globin gene

EU orphan designation number: EU/3/14/1263   
Active ingredient: Autologous CD34+ haematopoietic stem cells transduced with lentiviral vector encoding the human beta A-T87Q-globin gene
Indication: Treatment of sickle cell disease
Sponsor: bluebird bio (Germany) GmbH
Josephspitalstraße 15, 80331 München, Deutschland

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
7/07/2014 Orphan designation EMA/OD/184/13 (2014)2969 of 29/04/2014
27/07/2018 Transfer of orphan designation EMA/OD/184/13/T/01 (2018)5035 of 25/07/2018