Navigation path

Pharmaceuticals - Community Register

  

Community register of orphan medicinal products


GRANTED  

Product information

Autologous CD34+ cells transduced with a lentiviral vector containing the human ADA gene

EU orphan designation number: EU/3/13/1134   
Active ingredient: Autologous CD34+ cells transduced with a lentiviral vector containing the human ADA gene
Indication: Treatment of adenosine deaminase-deficient-severe combined immunodeficiency
Sponsor: Orchard Therapeutics Ltd
108 Cannon Street, London EC4N 6EU, United Kingdom

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
11/06/2013 Orphan designation EMA/OD/014/13 (2013)3669 of 7/06/2013
4/12/2017 Transfer of orphan designation EMA/OD/014/13/T/01 (2017)8250 of 30/11/2017
9/07/2018 Change of name and/or address of sponsor