Navigation path

Pharmaceuticals - Community Register

  

Community register of orphan medicinal products


GRANTED  

Product information

Autologous CD34+ cells transduced with a lentiviral vector containing the human ADA gene

EU orphan designation number: EU/3/13/1134   
Active ingredient: Autologous CD34+ cells transduced with a lentiviral vector containing the human ADA gene
Indication: Treatment of adenosine deaminase-deficient-severe combined immunodeficiency
Sponsor: Prof. Bobby Gaspar
UCL Institute of Child Health, 30 Guilford Street, London, WC1N 1EH, United Kingdom

   Public summary of scientific opinion    

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
11/06/2013 Orphan Designation EMA/OD/014/13 (2013)3669 of 07/06/2013