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Community register of orphan medicinal products


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Adeno-associated viral vector serotype 9 containing the human N-acetylglucosaminidase alpha gene

EU orphan designation number: EU/3/12/1095   
Active ingredient: Adeno-associated viral vector serotype 9 containing the human N-acetylglucosaminidase alpha gene
Indication: Treatment of mucopolysaccharidosis type IIIB (Sanfilippo B syndrome)
Sponsor: Laboratorios del Dr. Esteve, S.A.
Av. Mare de Déu de Montserrat 221, E-08041 Barcelona, España

   Public summary of scientific opinion    

 

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
28/01/2013 Centralised Orphan - Designation EMA/OD/150/12 (2013)484 of 24/01/2013