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Community register of orphan medicinal products


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Autologous CD34+ haematopoietic stem cells transduced with lentiviral vector encoding the human betaA-T87Q-globin gene

EU orphan designation number: EU/3/12/1091   
Active ingredient: Autologous CD34+ haematopoietic stem cells transduced with lentiviral vector encoding the human betaA-T87Q-globin gene
Indication: Treatment of beta-thalassaemia intermedia and major
Sponsor: bluebird bio France
155 rue du Faubourg Saint-Denis, 75010 Paris, France

   Public summary of scientific opinion    

 

European Commission proceduresGoto top of the page

Close date procedure Procedure type EMEA number Decision summary publ decision docs annex
28/01/2013 Centralised Orphan - Designation EMA/OD/146/12 (2013)480 of 24/01/2013
23/01/2014 Centralised Orphan - Change of address